March 11 (Reuters) - Regenxbio said on Wednesday that interim data from a early-to-mid stage study of its experimental gene therapy in patients with Duchenne muscular dystrophy showed continued ...

UCLA researchers use lipid nanoparticles to insert full CFTR gene into airway cells, restoring function and opening new avenues for CF therapy.

Gene-set analysis seeks to identify the biological mechanisms underlying groups of genes with shared functions. Large language models (LLMs) have shown promise in generating functional descriptions ...

Researchers use long-read genome sequencing to discover 33% more structural variants and 38% more tandem repeats linked to autism spectrum disorder.

Researchers at the Nora Eccles Harrison Cardiovascular Research and Training Institute, University of Utah, and the University of Utah School of Medicine, have demonstrated that a gene therapy can ...

Researchers at the University of California San Diego have identified new genetic variants associated with autism spectrum disorder (ASD) by using long-read whole genome sequencing (LR-WGS), an ...

This article was review by Paul Sternberg, PhD from the California Institute of Technology and the Gene Ontology Consortium (GOC). Stay up to date on the latest science with Brush Up Summaries. The ...

The liver of a 56-year-old male patient was severely damaged. Suffering from chronic hepatitis B and heavy alcohol consumption, he developed severe liver failure. Without a transplant, survival was ...

Antibiotic susceptibility in resistant bacteria is not static. New research shows that bacteria harboring resistance genes may respond differently to antibiotics if they are tested under conditions ...

A science communicator transformed textbook genetics into an interactive card game that can teach students the basics of ...