The investigational gene therapy SGT-003 is showing early signs of safety and efficacy for Duchenne muscular dystrophy in a ...
Experimental therapy RT1999 will soon be tested in the UK EXPERTS-ALS platform trial designed to rapidly screen potential ALS treatments.
The Muscular Dystrophy Association (MDA) concluded its 2026 MDA Clinical & Scientific Conference yesterday, convening over 2,400 attendees from 40 countries to help shape the future of neuromuscular ...
The president and CEO of the Muscular Dystrophy Association talks about what she's most excited about in neuromuscular ...
Data presented at the 2026 Muscular Dystrophy Association meeting could have readthroughs to companies developing therapies for spinal muscular atrophy, Duchenne muscular dystrophy and Becker muscular ...
Jul. 2—Three recent drug busts have turned up MDA, a psychedelic stimulant, in St. Lawrence County. MDA is often called sassafras or Sally. It is similar to MDMA, which is often called ecstasy or ...
The Muscular Dystrophy Association (MDA)’s Venture Philanthropy arm has injected $1.2 million into Valerion Therapeutics’ myotubular myopathy (MTM) pipeline, funding the firm to continue its ...
MDA's 75-year progress includes gene discoveries and drug approvals for DMD and SMA, emphasizing the importance of sustained research funding. Advocacy efforts target Medicaid coverage, newborn ...
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