Myotonic dystrophy type 1 incurs high healthcare costs, driven by age and comorbidities like cardiac and respiratory issues. Early detection and integrated management of multisystemic complications ...

Comedian Gilbert Gottfried died on Tuesday after a long illness, his family announced. His publicist revealed in a statement to multiple publications, including People, that Gottfried had “recurrent ...

Gilbert Gottfried’s family is asking for the late celebrity's fans to show their support by donating money for research of the disease that took his life. On Wednesday, a tweet shared from the ...

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AOC 1001 continues to be generally well tolerated; Avidity provides more information on the rare serious adverse event in a single participant that led to the partial clinical hold AOC 1001 top-line ...

Gilbert Gottfried's family released the final video of the comedian shot hours before he was rushed to the hospital. In the hours before his death, the comedian had been filming an episode of his ...

Dyne Therapeutics announces FDA Fast Track designation for DYNE-101, targeting myotonic dystrophy type 1 with potential accelerated approval in 2026. Dyne Therapeutics has announced that its ...

- Patient-reported outcomes support clinical meaningfulness of improvements in function and strength - - Meaningful improvements in overall disease burden reported by both patients and physicians - ...