The baby saved from a rare disease by a first-ever personalized gene fix has reached a big milestone, taking his first steps ahead of Christmas. KJ Muldoon is walking and getting ready to celebrate ...
A baby born with a rare and life-threatening genetic disorder has taken his first steps after receiving a groundbreaking, ...
A miracle baby who was treated with a pioneering gene-therapy at CHOP has reached a major milestone as he took his first ...
Interesting Engineering on MSN
Home for Christmas: Baby treated with world-first CRISPR therapy takes first steps
Today, he is learning to walk at home with his family. His first steps follow a medical first that changed the course of his ...
A toddler who received the first-of-its-kind gene therapy for a potentially fatal disease has taken his first steps at 16 ...
On a video call in early September, Sarah Tabrizi first saw the data that she and other researchers studying Huntington’s ...
JABSOM Cell and Molecular Biology researcher Dr. Jesse Owens has spent the better part of two decades chasing a vision that ...
Vence L. Bonham Jr., Acting Deputy Director at the National Human Genome Research Institute (NHGRI) and an investigator in the National Human Genome Research Institute’s (NHGRI) Division of Intramural ...
DMD gene therapy faces challenges in safety, efficacy, and long-term outcomes, despite FDA approval of delandistrogene moxeparvovec. Future strategies focus on novel AAV capsids, dual/triple vector ...
Alison Clare has received funding from the Wellcome Trust and the Medical Research Council. Her position is currently funded by National Institute for Health and Care Research (NIHR) Biomedical ...
ZURICH (Reuters) - Roche is buying U.S.-based gene therapy specialist Spark Therapeutics for $4.3 billion after developments in this area convinced the Swiss drugmaker to "step up", Chief Executive ...
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