Gene mutations behind serious bone marrow conditions identified

Inherited bone marrow failure syndrome, or IBMFS, describes a group of disorders in which inherited genetic abnormalities ...
FOX13 Memphis

St. Jude researchers receive $28.5 million to develop gene-editing treatment for children with rare diseases

For children born with rare inherited bone marrow disorders, treatment can often mean chemotherapy, a bone marrow transplant, ...

Bone marrow transplant is not a last resort for thalassemia: Doctors reveal the myths, facts and realities families often overlook

A bone marrow transplant can effectively cure thalassemia major, moving beyond traditional care methods. This life-changing ...
News-Medical.Net

New study reveals genetic drivers of inherited bone marrow failure syndrome

Inherited bone marrow failure syndrome, or IBMFS, describes a group of disorders in which inherited genetic abnormalities ...
News Medical

Breakthrough in blood stem cell development offers hope for leukemia and bone marrow failure

And the discovery could soon lead to personalized treatments for children with leukemia and bone marrow failure disorders. The research, led by Murdoch Children's Research Institute (MCRI) and ...

Utah girl Emma Meline was diagnosed with severe aplastic anemia days before Christmas; her 2-year-old sister became her perfect bone marrow match

Emma Meline, a young girl diagnosed with severe aplastic anemia right before Christmas, found hope in her little sister Lucy.
Medical Xpress

Bone Marrow Failure Disorders

A new treatment that involves growing a patient's immune cells and then infusing them back into their body has shown promise for people with the rare blood disorder aplastic anemia. Results from the ...